ApprovedMitochondrial / Barth syndrome

Elamipretide

Brand examples:SS-31MTP-131

Class
Mitochondrial cardiolipin binder
Route
SC injection
Frequency
Once daily in approved labeling
GLP-1 relevance
No

How it works

Mitochondrial cardiolipin binder (mitochondria-targeted tetrapeptide)

Approved & studied uses

Improving muscle strength in adult and pediatric patients with Barth syndrome weighing at least 30 kg, per US labeling.

Regulatory status

Approved (US, 2025; marketed as FORZINITY). Approval status varies by country.

Safety notes

Prescription-only. Dose and schedule are set by your prescriber; Peptimize does not recommend or adjust them.

Sources

Educational reference only. This page does not provide diagnosis, dosing, titration or treatment recommendations. Peptimize does not recommend or adjust any medication schedule - that is between you and your prescriber.